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EMA validates MAA for valoctocogene roxaparvovec.

Read time: 1 mins
Last updated:28th Jul 2021
Published:16th Jul 2021
BioMarin Pharmaceutical Inc. announced that the European Medicines Agency (EMA) validated the Company's Marketing Authorization Application (MAA) for its investigational gene therapy, valoctocogene roxaparvovec, for adults with severe haemophilia A. With this validation the MAA review can now commence. A CHMP opinion is anticipated in the first half of 2022.
Condition: Haemophilia A
Type: drug
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