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FDA approves Dojolvi for the treatment of pediatric and adult patients with molecularly confirmed long-chain fatty acid oxidation disorders. _Ultragenyx.

Read time: 1 mins

Published:4th Jul 2020

Ultragenyx Pharmaceutical Inc. announced that the FDA has approved Dojolvi (triheptanoin) as a source of calories and fatty acids for the treatment of pediatric and adult patients with molecularly confirmed long-chain fatty acid oxidation disorders (LC-FAOD). LC-FAOD are a group of rare, lifelong and life-threatening genetic disorders in which the body is unable to convert long-chain fatty acids into energy. Dojolvi is a highly purified, synthetic, 7-carbon fatty acid triglyceride specifically designed to provide medium-chain, odd-carbon fatty acids as an energy source and metabolite replacement for people with LC-FAOD.

Condition: Fatty Acid Oxidation Disorders

Type: drug

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