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Read time: 17 mins
Last updated: 03 Jul 2019
Published: 16 Oct 2020

4.1 Therapeutic indications

Miglustat Capsules are indicated for the oral treatment of adult patients with mild to moderate type 1 Gaucher disease. Miglustat Capsules may be used only in the treatment of patients for whom enzyme replacement therapy is unsuitable (see sections 4.4 and 5.1).

Miglustat Capsules are indicated for the treatment of progressive neurological manifestations in adult patients and paediatric patients with Niemann-Pick type C disease (see sections 4.4, and 5.1).

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