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Journal

A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II.

Read time: 1 mins
Published:1st Jan 2016
Author: Muenzer J, Hendriksz CJ, Fan Z, Vijayaraghavan S, Perry V, Santra S, et al.
Availability: Free full text
Ref.:Genet Med. 2016 Jan;18(1):73-81.
DOI:10.1038/gim.2015.36.
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